April 15, 2024
See a letter to the Angelman community. Ultragenyx reported positive interim data from the ongoing Phase 1/2 study in patients living with deletion genotype Angelman syndrome after treatment with investigational GTX-102. From company press release: “The totality of these […]
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March 7, 2024
Washington D.C., – The Angelman Syndrome Foundation (ASF) and the Foundation for Angelman Syndrome Therapeutics (FAST) are hosting the inaugural Angelman Syndrome (AS) Congressional Advocacy Day in Washington, D.C. Angelman syndrome advocates from all corners of the country will head […]
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January 13, 2024
The Angelman Syndrome Foundation is proud to announce a new collaboration with Cedars-Sinai Guerin Children’s to launch a new clinic for patients with Angelman syndrome, a rare neuro-genetic disorder. The clinic is led by Cesar Ochoa-Lubinoff, MD, MPH, director of […]
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October 13, 2023
The Angelman Syndrome Foundation and the Dup15q Alliance are proud to announce plans to launch a new clinic at Children’s Hospital of Philadelphia (CHOP) to better serve the Angelman and Dup15q communities. “We are excited to join other Angelman and […]
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